Biochemical, histological and functional correction of mucopolysaccharidosis type IIIB by intra-cerebrospinal fluid gene therapy.
2015
Ribera, A., V. Haurigot, et al. (2015).
Hum Mol Genet 24(7): 2078-2095.
2015
Ribera, A., V. Haurigot, et al. (2015).
Hum Mol Genet 24(7): 2078-2095.