2023
Albini S et Al. « Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy » International Journal of Molecular Sciences, 24,11421
Aronson SJ et Al.
« What's next in gene therapy for Crigler-Najjar syndrome? »
Expert opinion on biological therapy 23, 119-121.
Barbon E et Al.
« Development of a dualIP – 11/12/202339hybrid AAV vector for endothelial-targeted expression of von Willebrand factor. »
Gene therapy 30, 245-254.
Berling E et Al.
« Gene therapy review: Duchenne muscular dystrophy case study »
Revue neurologique 179, 90-105
Brusson M et Al.
« Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies. »
Molecular therapy Nucleic acids 32, 229-246.