- 24 May 2019 Towards a clinical trial for gamma-sarcoglycanopathy, limb-girdle muscular dystrophy
- 25 February 2019 Clinical Proof-of-Concept Data for OTL-102 for the Treatment of X-CGD
- 10 December 2018 Genethon announces dosing of the first patient with Crigler–Najjar Syndrome
Created in 1990 by AFM-TELETHON, Genethon is fully dedicated to the design and development of gene therapy treatments for rare diseases. Its objective is to provide these innovative treatments to patients affected with rare disorders.
Genethon is developing therapies for rare neuromuscular diseases, immune system or blood disorders, eye disorders and liver diseases.