Généthon - Gene therapy treatments for rare diseases

Gene therapy treatments for rare diseases

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Diseases of the muscles, immune system, blood, retina…

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An integrated structure: from research to clinical trials

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Globally unrivalled bioproduction capacities

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International partners

Breaking news

26 January 2012 Genethon Lecture Series
17 January 2012 Fulvio Mavilio, the internationally acknowledged expert in gene therapy for rare diseases, is appointed as Genethon's new Scientific Director
12 January 2012 Gene therapy : Encouraging results in a Phase I clinical trial in limb-girdle muscular dystrophy type 2C

All the latest news

Pipeline

Research Pre-clinical phase Phase I or I/II

Gamma-sarcoglycanopathy (IM administration)

Wiskott-Aldrich Syndrome (WAS)

Chronic Granulomatous Disease

Duchenne Muscular Dystrophy

Leber’s Hereditary Optic Neuropathy

All the products

Bioproduction

Genethon Bioprod, the world’s largest center for the production of clinical grade gene therapy products