Advancing gene therapytreatments fore rare diseases

Created in 1990 by AFM-TELETHON, Genethon is fully dedicated to the design, development and production of gene therapy treatments for rare diseases. Its objective is to provide these innovative treatments to patients affected with rare disorders.

Genethon is developing therapies for rare neuromuscular diseases, immune system or blood disorders, eye disorders, liver and nervous system diseases.


Our mission