Monday July 15th, 2013: “Design and delivery of micro-dystrophins for DMD therapy” Pr Jeffrey S. Chamberlain, University of Washington School of Medicine, Depts. of Neurology, Medicine and Biochemistry, Seattle, USA
Friday July 12th, 2013: “HIV integration and regulation” Dr Frederic D. Bushman, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, USA.
Wednesday May 29th, 2013: “Gene therapy for beta-thalassemia: The challenge of a new cure” Dr Giuliana Ferrari, HSR-TIGET, Universita Vita-Salute San Raffaele, Milan, Italy
Tuesday February 19th,2013 : “Identification of tumorigenic pathways from large-scale genomic data” Dr Silvio Bicciato, Center for Genome Research, Department of Life Sciences, University of Modena and Reggio Emilia, Italy
Wednesday February 13th,2013 : « Production of AAV vectors in Baculoviruses » Dr Robert M. Kotin, National Institutes of Health (NIH), Laboratory of Molecular Virology and Gene Therapy, Bethesda, US.
This year’s Telethon will remain the challenge of all challenges: the challenge of donors and volunteers in the face of crisis, the challenge of researchers and families in the face of disease … Together, we have tackled them, with determination and courage, all united by the same desire: win! The counter of Telethon 2012 stopped … [Read more]
Gene therapies advance, but some see manufacturing challenges
“Gene therapy has traveled a long and winding road to the clinic. The field famously hit a major roadblock 13 years ago when the teenager Jesse Gelsinger suffered a fatal immune reaction in response to a gene therapy product designed to correct his rare liver disease, leading to a perception…”
Author : Elie Dolgin