Thursday April 3rd, 2014: “Gene Therapy for Haemophilia B” Prof. Amit Nathwani (Centre Director of the Katharine Dormandy Haemophilia Centre, Katharine Dormandy Haemophilia Centre and Thrombosis Unit. Royal Free Hospital , London, United Kingdom)
Friday December 13th, 2013: « Causes of rimmed vacuolar muscle diseases – and the example of mutated DNAJB6 » Pr Bjarne Udd (Tampere University and University Hospital, Neuromuscular Research Unit, Tampere, Finland).
Le jeudi 12 décembre 2013 : « Gene therapy of mucopolysaccharidosis IIIA » Pr Fatima Bosch (Professor of the Faculty of the Universitat Autonoma de Barcelona and Director of the CBATEG (Center of Animal Biotechnology and Gene Therapy), Bellatera, Barcelona, Spain
Friday November 22th, 2013: « Role of autophagy in muscular dystrophies and in cardiomyopathies » Marco Sandri, MD (University of Padova, Department of Biomedical Science, Italy and Dulbecco Telethon Institute at Venetian Institute of Molecular Medicine, Padova, Italy)
Read the article (PDF in French)
The AFM-Telethon laboratory has been certified as a pharmaceutical manufacturer by ANSM, thus becoming the first not-for-profit laboratory.
- Read the article (in French) : www.industrie.com/pharma
Unique in the world, this laboratory, financed by the Telethon, has just opened south of Paris. It will manufacture products for gene therapy treatments on a large scale.
- Read the article : www.lepoint.fr