Scientific Publications 2013

  1. 1. Aiuti, A., L. Biasco, et al. (2013). “Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.” Science 341(6148): 1233151.
  2. 2. Andre-Schmutz, I., L. Dal-Cortivo, et al. (2013). “Genotoxic signature in cord blood cells of newborns exposed in utero to a Zidovudine-based antiretroviral combination.” J Infect Dis 208(2): 235-243.
  3. 3. Ben Abdelwahed, R., J. Cosette, et al. (2013). “Lymphoma B-cell responsiveness to CpG-DNA depends on the tumor microenvironment.” J Exp Clin Cancer Res 32: 18.
  4. 4. Ben Abdelwahed, R., S. Donnou, et al. (2013). “Preclinical study of Ublituximab, a Glycoengineered anti-human CD20 antibody, in murine models of primary cerebral and intraocular B-cell lymphomas.” Invest Ophthalmol Vis Sci 54(5): 3657-3665.
  5. 5. Biondi, O., M. Villemeur, et al. (2013). “Dual effects of exercise in dysferlinopathy.” Am J Pathol 182(6): 2298-2309.
  6. 6. Blandin, G., S. Marchand, et al. (2013). “A human skeletal muscle interactome centered on proteins involved in muscular dystrophies: LGMD interactome.” Skelet Muscle 3(1): 3.
  7. 7. Boisgerault, F., D. A. Gross, et al. (2013). “Prolonged gene expression in muscle is achieved without active immune tolerance using MicrorRNA 142.3p-regulated rAAV gene transfer.” Hum Gene Ther 24(4): 393-405.
  8. 8. Cavazza, A., F. Cocchiarella, et al. (2013). “Self-inactivating MLV vectors have a reduced genotoxic profile in human epidermal keratinocytes.” Gene Ther.
  9. 9. Cavazza, A., A. Moiani, et al. (2013). “Mechanisms of retroviral integration and mutagenesis.” Hum Gene Ther 24(2): 119-131.
  10. 10. Charrier, S., M. Blundell, et al. (2013). “Wiskott-Aldrich syndrome protein-deficient hematopoietic cells can be efficiently mobilized by granulocyte colony-stimulating factor.” Haematologica 98(8): 1300-1308.
  11. 11. Coluccio, A., F. Miselli, et al. (2013). “Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination.” Mol Ther 21(9): 1695-1704.
  12. 12. Daussy, C., D. Damotte, et al. (2013). “CD4:CD8 T-Cell ratio differs significantly in diffuse large B-cell lymphomas from other lymphoma subtypes independently from lymph node localization.” Int Trends Immunity 1(2): 45-48.
  13. 13. Decostre, V., A. Vignaud, et al. (2013). “Longitudinal in vivo muscle function analysis of the DMSXL mouse model of myotonic dystrophy type 1.” Neuromuscul Disord.
  14. 14. Denard, J., B. Marolleau, et al. (2013). “C-reactive protein (CRP) is essential for efficient rAAV-1 and rAAV-6 systemic transduction in mice.” J Virol.
  15. 15. Di Nunzio, F., T. Fricke, et al. (2013). “Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication.” Virology 440(1): 8-18.
  16. 16. Fayssoil, A., G. Renault, et al. (2013). “Cardiac characterization of mdx mice using high-resolution doppler echocardiography.” J Ultrasound Med 32(5): 757-761.
  17. 17. Fayssoil, A., G. Renault, et al. (2013). “Cardiac Characterization of sgca-Null Mice Using High Resolution Echocardiography.” Neurol Int 5(4): e22.
  18. 18. Fenard, D., S. Genries, et al. (2013). “Infectivity enhancement of different HIV-1-based lentiviral pseudotypes in presence of the cationic amphipathic peptide LAH4-L1.” J Virol Methods 189(2): 375-378.
  19. 19. Fenard, D., D. Ingrao, et al. (2013). “Vectofusin-1, a new viral entry enhancer, strongly promotes lentiviral transduction of human hematopoietic stem cells.” Mol Ther Nucleic Acids 2: e90.
  20. 20. Fisson, S., H. Ouakrim, et al. (2013). “Cytokine profile in human eyes: contribution of a new cytokine combination for differential diagnosis between intraocular lymphoma or uveitis.” PLoS One 8(2): e52385.
  21. 21. Frih, H., L. Bensaci, et al. (2013). “Freund’s complete adjuvant (FCA) could reverse the depressive-like symptoms induced by chronic mild stress (CMS) in mice.” J Neurol Neurophysiol 4(1): 143-151.
  22. 22. Hirsch, M. L., C. Li, et al. (2013). “Oversized AAV Transduction is Mediated via a DNA-PKcs Independent, Rad51C-dependent Repair Pathway.” Mol Ther.
  23. 23. Hui, D. J., E. Basner-Tschakarjan, et al. (2013). “Modulation of CD8 T cell responses to AAV vectors with IgG-derived MHC class II epitopes.” Mol Ther.
  24. 24. Joubert, R., A. Vignaud, et al. (2013). “Site-specific Mtm1 mutagenesis by an AAV-Cre vector reveals that myotubularin is essential in adult muscle.” Hum Mol Genet 22(9): 1856-1866.
  25. 25. Kaufmann, K. B., H. Buning, et al. (2013). “Gene therapy on the move.” EMBO Mol Med.
  26. 26. Lawlor, M. W., D. Armstrong, et al. (2013). “Enzyme replacement therapy rescues weakness and improves muscle pathology in mice with X-linked myotubular myopathy.” Hum Mol Genet 22(8): 1525-1538.
  27. 27. Marek, M., C. Romier, et al. (2013). “Baculovirus VP1054 Is an Acquired Cellular PURalpha, a Nucleic Acid-Binding Protein Specific for GGN Repeats.” J Virol 87(15): 8465-8480.
  28. 28. Masat, E., G. Pavani, et al. (2013). “Humoral immunity to AAV vectors in gene therapy: challenges and potential solutions.” Discov Med 15(85): 379-389.
  29. 29. Mingozzi, F., X. M. Anguela, et al. (2013). “Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys.” Sci Transl Med 5(194): 194ra192.
  30. 30. Moiani, A., A. Miccio, et al. (2013). “Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors.” PLoS One 8(1): e55721.
  31. 31. Monjaret, F., L. Suel-Petat, et al. (2013). “The phenotype of dysferlin-deficient mice is not rescued by adeno-associated virus-mediated transfer of anoctamin 5.” Hum Gene Ther Clin Dev 24(2): 65-76.
  32. 32. Nahdi, I., R. B. Abdelwahed, et al. (2013). “Herpesvirus detection and cytokine levels (IL-10, IL-6, and IFN-gamma) in ocular fluid from tunisian immunocompetent patients with uveitis.” J Med Virol.
  33. 33. Paldi, A. (2013). “Effects of the in vitro manipulation of stem cells: epigenetic mechanisms as mediators of induced metabolic fluctuations.” Epigenomics 5(4): 429-437.
  34. 34. Roudaut, C., F. Le Roy, et al. (2013). “Restriction of Calpain3 Expression to the Skeletal Muscle Prevents Cardiac Toxicity and Corrects Pathology in a Murine Model of Limb-Girdle Muscular Dystrophy.” Circulation.
  35. 35. Saliba, J., S. Hamidi, et al. (2013). “Heterozygous and homozygous JAK2(V617F) states modeled by induced pluripotent stem cells from myeloproliferative neoplasm patients.” PLoS One 8(9): e74257.
  36. 36. Silva, A. K., C. Richard, et al. (2013). “Xyloglucan-derivatized films for the culture of adherent cells and their thermocontrolled detachment: a promising alternative to cells sensitive to protease treatment.” Biomacromolecules 14(2): 512-519.
  37. 37. Touitou, V., C. Daussy, et al. (2013). “Naturally occurring CD4+CD25+Foxp3+ regulatory T cells participate in but do not govern immune escape in primary intraocular lymphoma.” Int Trends Immunity 1(4): 62-68.
  38. 38. Tremblay, J. P., X. Xiao, et al. (2013). “Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases.” Mol Ther 21(2): 266-268.
  39. 39. van Zwieten, R. W., S. Puttini, et al. (2013). “Assessing dystrophies and other muscle diseases at the nanometer scale by atomic force microscopy.” Nanomedicine (Lond).
  40. 40. Vignier, N., F. Amor, et al. (2013). “Distinctive serum miRNA profile in mouse models of striated muscular pathologies.” PLoS One 8(2): e55281.
  41. 41. Zerbato, M., N. Holic, et al. (2013). “The brown algae Pl.LSU/2 group II intron-encoded protein has functional reverse transcriptase and maturase activities.” PLoS One 8(3): e58263.