Genethon and Wake Forest University School of Medicine (North Carolina) announce their collaboration for a preclinical gene therapy trial

Evry (France), March 8th, 2011 – Genethon (the not-for-profit biotherapy lab funded by the French Muscular Dystrophy Association (Association Française contre les Myopathies, AFM) with donations from France’s annual Telethon) and Wake Forest University School of Medicine (Winston Salem, North Carolina, USA) today announced that they are to collaborate on the preclinical development of a gene therapy for myotubular myopathy. This rare genetic disease is a very severe congenital myopathy which affects skeletal muscles and leads to respiratory failure from birth.