Publications scientifiques 2013

  1. 1. Aiuti, A., L. Biasco, et al. (2013). « Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome. » Science 341(6148): 1233151.
  2. 2. Andre-Schmutz, I., L. Dal-Cortivo, et al. (2013). « Genotoxic signature in cord blood cells of newborns exposed in utero to a Zidovudine-based antiretroviral combination. » J Infect Dis 208(2): 235-243.
  3. 3. Ben Abdelwahed, R., J. Cosette, et al. (2013). « Lymphoma B-cell responsiveness to CpG-DNA depends on the tumor microenvironment. » J Exp Clin Cancer Res 32: 18.
  4. 4. Ben Abdelwahed, R., S. Donnou, et al. (2013). « Preclinical study of Ublituximab, a Glycoengineered anti-human CD20 antibody, in murine models of primary cerebral and intraocular B-cell lymphomas. » Invest Ophthalmol Vis Sci 54(5): 3657-3665.
  5. 5. Biondi, O., M. Villemeur, et al. (2013). « Dual effects of exercise in dysferlinopathy. » Am J Pathol 182(6): 2298-2309.
  6. 6. Blandin, G., S. Marchand, et al. (2013). « A human skeletal muscle interactome centered on proteins involved in muscular dystrophies: LGMD interactome. » Skelet Muscle 3(1): 3.
  7. 7. Boisgerault, F., D. A. Gross, et al. (2013). « Prolonged gene expression in muscle is achieved without active immune tolerance using MicrorRNA 142.3p-regulated rAAV gene transfer. » Hum Gene Ther 24(4): 393-405.
  8. 8. Cavazza, A., F. Cocchiarella, et al. (2013). « Self-inactivating MLV vectors have a reduced genotoxic profile in human epidermal keratinocytes. » Gene Ther.
  9. 9. Cavazza, A., A. Moiani, et al. (2013). « Mechanisms of retroviral integration and mutagenesis. » Hum Gene Ther 24(2): 119-131.
  10. 10. Charrier, S., M. Blundell, et al. (2013). « Wiskott-Aldrich syndrome protein-deficient hematopoietic cells can be efficiently mobilized by granulocyte colony-stimulating factor. » Haematologica 98(8): 1300-1308.
  11. 11. Coluccio, A., F. Miselli, et al. (2013). « Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination. » Mol Ther 21(9): 1695-1704.
  12. 12. Daussy, C., D. Damotte, et al. (2013). « CD4:CD8 T-Cell ratio differs significantly in diffuse large B-cell lymphomas from other lymphoma subtypes independently from lymph node localization. » Int Trends Immunity 1(2): 45-48.
  13. 13. Decostre, V., A. Vignaud, et al. (2013). « Longitudinal in vivo muscle function analysis of the DMSXL mouse model of myotonic dystrophy type 1. » Neuromuscul Disord.
  14. 14. Denard, J., B. Marolleau, et al. (2013). « C-reactive protein (CRP) is essential for efficient rAAV-1 and rAAV-6 systemic transduction in mice. » J Virol.
  15. 15. Di Nunzio, F., T. Fricke, et al. (2013). « Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication. » Virology 440(1): 8-18.
  16. 16. Fayssoil, A., G. Renault, et al. (2013). « Cardiac characterization of mdx mice using high-resolution doppler echocardiography. » J Ultrasound Med 32(5): 757-761.
  17. 17. Fayssoil, A., G. Renault, et al. (2013). « Cardiac Characterization of sgca-Null Mice Using High Resolution Echocardiography. » Neurol Int 5(4): e22.
  18. 18. Fenard, D., S. Genries, et al. (2013). « Infectivity enhancement of different HIV-1-based lentiviral pseudotypes in presence of the cationic amphipathic peptide LAH4-L1. » J Virol Methods 189(2): 375-378.
  19. 19. Fenard, D., D. Ingrao, et al. (2013). « Vectofusin-1, a new viral entry enhancer, strongly promotes lentiviral transduction of human hematopoietic stem cells. » Mol Ther Nucleic Acids 2: e90.
  20. 20. Fisson, S., H. Ouakrim, et al. (2013). « Cytokine profile in human eyes: contribution of a new cytokine combination for differential diagnosis between intraocular lymphoma or uveitis. » PLoS One 8(2): e52385.
  21. 21. Frih, H., L. Bensaci, et al. (2013). « Freund’s complete adjuvant (FCA) could reverse the depressive-like symptoms induced by chronic mild stress (CMS) in mice. » J Neurol Neurophysiol 4(1): 143-151.
  22. 22. Hirsch, M. L., C. Li, et al. (2013). « Oversized AAV Transduction is Mediated via a DNA-PKcs Independent, Rad51C-dependent Repair Pathway. » Mol Ther.
  23. 23. Hui, D. J., E. Basner-Tschakarjan, et al. (2013). « Modulation of CD8 T cell responses to AAV vectors with IgG-derived MHC class II epitopes. » Mol Ther.
  24. 24. Joubert, R., A. Vignaud, et al. (2013). « Site-specific Mtm1 mutagenesis by an AAV-Cre vector reveals that myotubularin is essential in adult muscle. » Hum Mol Genet 22(9): 1856-1866.
  25. 25. Kaufmann, K. B., H. Buning, et al. (2013). « Gene therapy on the move. » EMBO Mol Med.
  26. 26. Lawlor, M. W., D. Armstrong, et al. (2013). « Enzyme replacement therapy rescues weakness and improves muscle pathology in mice with X-linked myotubular myopathy. » Hum Mol Genet 22(8): 1525-1538.
  27. 27. Marek, M., C. Romier, et al. (2013). « Baculovirus VP1054 Is an Acquired Cellular PURalpha, a Nucleic Acid-Binding Protein Specific for GGN Repeats. » J Virol 87(15): 8465-8480.
  28. 28. Masat, E., G. Pavani, et al. (2013). « Humoral immunity to AAV vectors in gene therapy: challenges and potential solutions. » Discov Med 15(85): 379-389.
  29. 29. Mingozzi, F., X. M. Anguela, et al. (2013). « Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys. » Sci Transl Med 5(194): 194ra192.
  30. 30. Moiani, A., A. Miccio, et al. (2013). « Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors. » PLoS One 8(1): e55721.
  31. 31. Monjaret, F., L. Suel-Petat, et al. (2013). « The phenotype of dysferlin-deficient mice is not rescued by adeno-associated virus-mediated transfer of anoctamin 5. » Hum Gene Ther Clin Dev 24(2): 65-76.
  32. 32. Nahdi, I., R. B. Abdelwahed, et al. (2013). « Herpesvirus detection and cytokine levels (IL-10, IL-6, and IFN-gamma) in ocular fluid from tunisian immunocompetent patients with uveitis. » J Med Virol.
  33. 33. Paldi, A. (2013). « Effects of the in vitro manipulation of stem cells: epigenetic mechanisms as mediators of induced metabolic fluctuations. » Epigenomics 5(4): 429-437.
  34. 34. Roudaut, C., F. Le Roy, et al. (2013). « Restriction of Calpain3 Expression to the Skeletal Muscle Prevents Cardiac Toxicity and Corrects Pathology in a Murine Model of Limb-Girdle Muscular Dystrophy. » Circulation.
  35. 35. Saliba, J., S. Hamidi, et al. (2013). « Heterozygous and homozygous JAK2(V617F) states modeled by induced pluripotent stem cells from myeloproliferative neoplasm patients. » PLoS One 8(9): e74257.
  36. 36. Silva, A. K., C. Richard, et al. (2013). « Xyloglucan-derivatized films for the culture of adherent cells and their thermocontrolled detachment: a promising alternative to cells sensitive to protease treatment. » Biomacromolecules 14(2): 512-519.
  37. 37. Touitou, V., C. Daussy, et al. (2013). « Naturally occurring CD4+CD25+Foxp3+ regulatory T cells participate in but do not govern immune escape in primary intraocular lymphoma. » Int Trends Immunity 1(4): 62-68.
  38. 38. Tremblay, J. P., X. Xiao, et al. (2013). « Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases. » Mol Ther 21(2): 266-268.
  39. 39. van Zwieten, R. W., S. Puttini, et al. (2013). « Assessing dystrophies and other muscle diseases at the nanometer scale by atomic force microscopy. » Nanomedicine (Lond).
  40. 40. Vignier, N., F. Amor, et al. (2013). « Distinctive serum miRNA profile in mouse models of striated muscular pathologies. » PLoS One 8(2): e55281.
  41. 41. Zerbato, M., N. Holic, et al. (2013). « The brown algae Pl.LSU/2 group II intron-encoded protein has functional reverse transcriptase and maturase activities. » PLoS One 8(3): e58263.